This study is a prospective evaluation of children with Severe Combined Imm...
Status
Enrolling By Invitation
Location
University of Alabama at Birmingham
Start Date
2010-09-02
Trial ID
NCT01186913
Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA Gene
PHASE1
The aim of this study is to assess the safety and efficacy of autologous tr...